J 2019

Single-agent ibrutinib in RESONATE-2 (TM) and RESONATE (TM) versus treatments in the real-world PHEDRA databases for patients with chronic lymphocytic leukemia

SALLES, Gilles, Emmanuel BACHY, Lukáš SMOLEJ, Martin SIMKOVIC, Lucile BASEGGIO et. al.

Basic information

Original name

Single-agent ibrutinib in RESONATE-2 (TM) and RESONATE (TM) versus treatments in the real-world PHEDRA databases for patients with chronic lymphocytic leukemia

Authors

SALLES, Gilles (250 France, guarantor), Emmanuel BACHY (250 France), Lukáš SMOLEJ (203 Czech Republic), Martin SIMKOVIC (203 Czech Republic), Lucile BASEGGIO (250 France), Anna PANOVSKÁ (203 Czech Republic, belonging to the institution), Herve BESSON (372 Ireland), Nollaig HEALY (826 United Kingdom of Great Britain and Northern Ireland), Jamie GARSIDE (826 United Kingdom of Great Britain and Northern Ireland), Wafae IRAQI (250 France), Joris DIELS (56 Belgium), Corinna PICK-LAUER (276 Germany), Martin SPACEK (203 Czech Republic), Renata URBANOVA (203 Czech Republic), Daniel LYSAK, Ruben HERMANS (826 United Kingdom of Great Britain and Northern Ireland), Jessica LUNDBOM (826 United Kingdom of Great Britain and Northern Ireland), Evelyne CALLET-BAUCHU (250 France) and Michael DOUBEK (203 Czech Republic, belonging to the institution)

Edition

Annals of hematology, New York, Springer Verlag, 2019, 0939-5555

Other information

Language

English

Type of outcome

Článek v odborném periodiku

Field of Study

30205 Hematology

Country of publisher

United States of America

Confidentiality degree

není předmětem státního či obchodního tajemství

References:

Impact factor

Impact factor: 2.904

RIV identification code

RIV/00216224:14110/19:00112598

Organization unit

Faculty of Medicine

UT WoS

000497186800001

Keywords in English

Ibrutinib; Chronic lymphocytic leukemia; Real-world evidence; Randomized controlled trial; Progression-free survival; Overall survival

Tags

Tags

International impact, Reviewed
Změněno: 31/3/2020 22:16, Mgr. Pavla Foltynová, Ph.D.

Abstract

V originále

After analyzing treatment patterns in chronic lymphocytic leukemia (CLL) (objective 1), we investigated the relative effectiveness of ibrutinib versus other commonly used treatments (objective 2) in patients with treatment-naive and relapsed/refractory CLL, comparing patient-level data from two randomized registration trials with two real-world databases. Hazard ratios (HR) and 95% confidence intervals (CIs) were estimated using a multivariate Cox proportional hazards model, adjusted for differences in baseline characteristics. Rituximab-containing regimens were often prescribed in clinical practice. The most frequently prescribed regimens were fludarabine + cyclophosphamide + rituximab (FCR, 29.3%), bendamustine + rituximab (BR, 17.7%), and other rituximab-containing regimens (22.0%) in the treatment-naive setting (n = 604), other non-FCR/BR rituximab-containing regimens (38.7%) and non-rituximab-containing regimens (28.5%) in the relapsed/refractory setting (n = 945). Adjusted HRs (95% CI) for progression-free survival (PFS) and overall survival (OS), respectively, with ibrutinib versus real-world regimens were 0.23 (0.14-0.37; p < 0.0001) and 0.40 (0.22-0.76; p = 0.0048) in the treatment-naive setting, and 0.21 (0.16-0.27; p < 0.0001) and 0.29 (0.21-0.41; p < 0.0001) in the relapsed/refractory setting. When comparing real-world use of ibrutinib (n = 53) versus other real-world regimens in relapsed/refractory CLL (objective 3), adjusted HRs (95% CI) were 0.37 (0.22-0.63; p = 0.0003) for PFS and 0.53 (0.27-1.03; p < 0.0624) for OS. This adjusted analysis, based on nonrandomized patient data, suggests ibrutinib to be more effective than other commonly used regimens for CLL.